Advancing treatments for rare diseases together

AFMTéléthon supports EspeRare's drug development program in Duchenne

17Nov

AFM's review committee has decided to finance the development of Rimeporide in Duchenne muscular dystrophy (DMD).

Paris the 17th of July 2012, the French patient organization, a pioneer in funding rare disease research, has provided a positive review of EspeRare’s plan to test the efficacy of Rimeporide, a NHE-1 inhibitor, in a DMD animal model. As a consequent, AFMTéléthon has confirmed its intent to co-finance the evaluation of the therapeutic potential of Rimeporide. The animal testing is been performed by Dr. Kanneboyina Nagaraju specialized in DMD at the Children’s research institute in Washington DC in Professor Eric Hoffman's research center for genetic medicine.